Colin Farrell says his personal life has inspired him to launch a new foundation aimed at helping people with intellectual disabilities. The actor, 48, recently launched the Colin Farrell Foundation, ...
Researchers from the University of Tokyo reveal how the presynaptic Ube3a E3 ligase, a causal factor in Angelman syndrome, eliminates neural chat. The study helps find a better drug target for the ...
Henry Edberg dug through the play kitchen at his home in Rosemount before serving up the daily special to his older brother. “Vegetables are healthy, so I’m giving you the vegetables,” Henry, 3, told ...
This post was updated on April 24, 2019 to incorporate feedback from parents. Names have been changed to protect anonymity. Is this child happy? Source: Joel Frohlich (AI generated with Midjourney) ...
NOVATO, Calif., Jan. 03, 2024 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (RARE), a biopharmaceutical company focused on the development and commercialization of novel therapies for serious ...
Part 1 of HALOS trial evaluating ION582 has completed enrollment with results expected in mid-2024 ION582 has been generally well tolerated at all dose levels, and participants are continuing to Part ...
SARASOTA, Fla. and NOVATO, Calif., May 04, 2020 (GLOBE NEWSWIRE) -- GeneTx Biotherapeutics LLC and Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE), a biopharmaceutical company focused on the development ...
Company expects to complete Phase 3 Aspire study in the second half of 2026 Aurora study of GTX-102 in additional ages and genotypes on track to initiate in the second half of 2025 “The accelerated ...
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